Sickle Cell Disease: What's New with Transplant and Gene Therapy?

Please note: This symposium will be held virtually.

This symposium will discuss hematopoietic stem cell transplantation (HSCT) and gene therapy (GT) for sickle cell disease, with a focus on topics such as understanding new technologies related to HSCT/GT research, multidisciplinary collaborations among HSCT/GT experts, and the importance of including patients in the process of HSCT/GT research.

The target audience for this symposium is sickle cell disease researchers and health care providers.

If you are interested in the St. Jude Sickle Cell Disease Clinical Fellowship, please visit the fellowship web site for more information about the program, eligibility, and the application process. 

1. Identify possible areas of collaboration and potential collaborators in HSCT and GT research.
2. Describe multidisciplinary areas of need in new protocols and identify the types of experts who should be included to address them.
3. Implement strategies to encourage SCD patient involvement in HSCT/GT research protocols.

This symposium is free, but preregistration is required. You must preregister as an individual to be eligible for attendance or CME credit.

Registration is now open and will close on March 1, 2021. 

Other Information 

If you have any questions about this symposium, please contact Jane Stringellow at [email protected] or 901-595-6076. 

This activity has been planned and implemented in accordance with the accreditation requirements and policies of the Accreditation Council for Continuing Medical Education (ACCME) through the joint providership of St. Jude Children's Research Hospital and the Doris Duke Charitable Foundation. St. Jude Children's Research Hospital is accredited by the Accreditation Council for Continuing Medical Education (ACCME) to provide continuing medical education for physicians.

The faculty for this activity are listed below. Click to view the faculty member's financial disclosure information and bio. 

Allistair Abraham, MD
Attending Physician and Researcher, Division of Blood and Marrow Transplantation
Children's National Health System
Washington, MD

Daniel Bauer, MD, PhD
Assistant Professor, Pediatrics
Boston Children's Hospital
Boston, MA

Eric Bouhassira, PhD
Professor, Medicine and Cell Biology
Albert Einstein College of Medicine
Bronx, NY

Anjulika Chawla, MD
Associate Director Medical Affairs
Bluebird Bio
Providence, RI

Sindy Escobar-Alvarez, PhD
Senior Program Officer for Medical Research
Doris Duke Charitable Foundation
New York, NY

Haydar Frangoul, MD, MS
Medical Director of Pediatric Hematology/Oncology
TriStar Medical Group Children's Specialists
Nashville, TN

Donald Kohn, MD
Distinguished Professor
University of California, Los Angeles
Los Angeles, CA

Punam Malik, MD
Director, Cincinnati Comprehensive Sickle Cell Center
Cincinnati Children's Hospital
Cincinnati, OH

Matthew Porteus, MD, PhD
Professor of Pediatrics (Stem Cell Transplantation)
Stanford Medicine
Stanford, CA

Akshay Sharma, MBBS
Assistant Member
St. Jude Children's Research Hospital
Memphis , TN

John Tisdale, MD
Senior Investigator, Molecular and Clinical Hematology Branch
National Institutes of Health
Bethesda, MD

Tim Townes, PhD
Professor and Chair, Department of Biochemistry and Molecular Genetics
University of Alabama at Birmingham
Birmingham, AL

Shengdar Tsai, PhD
Assistant Member
St. Jude Children's Research Hospital
Memphis, TN

Fyodor Urnov, PhD
Scientific Director for Technology and Translation
Innovative Genomics Institute
Berkeley, CA

Mitchell J. Weiss, MD
Chair/Member
St. Jude Children's Research Hospital
MEMPHIS, TN

Lisbeth Welniak, PhD
Program Director
National Heart, Lung, and Blood Institute (NHLBI)
Bethesda, MD

Jonathan Yen, PhD
Director, Laboratory
St. Jude Children's Research Hospital
Memphis, TN

Tuesday, March 2, 2021